Tag: Thalassaemia

ENERGIZE: Mitapivat meets primary efficacy endpoint in thalassaemia

Presented By
Prof. Ali Taher, American University of Beirut, Lebanon
Trial
Phase 3, ENERGIZE
Conference
EHA 2024
Type
Peer-reviewed article

12 August 2024 14:26

Thalassaemia: Advances in conventional transplantation and gene therapy

Presented By
Prof. Josu de la Fuente, Imperial College London, UK
Conference
EBMT 2023
Type
Peer-reviewed article

15 June 2023 17:06

Long-term benefits from beti-cel in transfusion-dependent β-thalassaemia

Presented By
Prof. Mark Walters; Prof. Franco Locatelli
Trial
LTF-303
Conference
ASH 2022
Type
Peer-reviewed article

20 February 2023 13:14

Transfusion-dependent β-thalassaemia patients continue to benefit from luspatercept after 3 years of treatment

Presented By
Prof. Maria Capellini, University of Milan, Italy
Trial
Phase 3, BELIEVE
Conference
EHA 2022
Type
News article

1 July 2022 11:13

Single-dosed exa-cel leads to early and durable increase of foetal haemoglobin

Presented By
Prof. Franco Locatelli, University of Pavia, Italy
Trial
Phase 3, CLIMB THAL-111, CLIMB SCD-121
Conference
EHA 2022
Type
News article

1 July 2022 11:08

Luspatercept improved anaemia in patients with non-transfusion-dependent β-thalassaemia

Presented By
Prof. Ali Taher, American University of Beirut Medical Center, Lebanon
Trial
Phase 2, BEYOND
Conference
EHA 2021
Type
Peer-reviewed article

5 August 2021 15:43

Gene therapy: A promising approach for hereditary haemoglobinopathies

Presented By
Dr Haydar Frangoul, Sarah Cannon Research Institute, USA
Conference
EHA 2021
Type
Peer-reviewed article

5 August 2021 15:32

Promising CRISPR gene editing results in β-thalassaemia and sickle cell disease

Presented By
Dr Haydar Frangoul, Sarah Cannon Research Institute, USA
Trial
CLIMB THAL-111 & CLIMB SCD-121
Conference
ASH 2020
Type
Peer-reviewed article

18 February 2021 08:18

Erythroid maturation agent in patients with β-thalassaemia requiring regular RBC transfusions

Presented By
Prof. Olivier Hermine, Université de Paris, France
Trial
Phase 3, BELIEVE
Conference
ASH 2020
Type
Peer-reviewed article

18 February 2021 08:12

Mitapivat, a pyruvate kinase-R activator, in SCD is safe with early efficacy results

Presented By
Dr Kevin HM Kuo, Princess Margaret Cancer Centre, Canada
Trial
Phase 1
Conference
EHA 2020
Type
Peer-reviewed article

28 August 2020 15:46

Erythroferrone and skeletal changes associated with thalassaemia

Presented By
Dr Melanie Castro-Mollo, Icahn School of Medicine at Mount Sinai, USA
Conference
ASH 2019
Type
Peer-reviewed article

5 March 2020 22:39

Treating thalassemia twice, in mice

Presented By
Dr Antonella Nai, San Raffaele Scientific Institute, Italy
Conference
EHA 2019
Type
Peer-reviewed article

9 August 2019 22:03
site created by:   

© 2024 Medicom Medical Publishers.  All rights reserved. Terms and Conditions | Privacy Policy



HEAD OFFICE
Laarderhoogtweg 25
1101 EB Amsterdam
The Netherlands
T: +31 85 4012 560
E: publishers@medicom-publishers.com