Novel gene therapy leads to normal FIX activity levels in severe haemophilia B

Presented By

Dr Pratima Chowdary, Royal Free London NHS Foundation Trust, United Kingdom

Trial

Phase 1/2, B-AMAZE

Conference

ISTH 2020

8 September, 2020 14:31

Haemophilia gene therapy: progress and obstacles

Presented By

Prof. Amit Nathwani, University College London, United Kingdom

Trial

Review study

Conference

ISTH 2020

8 September, 2020 14:27