Tag: RNA Interference

HELIOS-B: Vutrisiran candidate for SoC in ATTR cardiomyopathy

Presented By
Prof. Marianna Fontana, University College London, UK
Trial
Phase 3, HELIOS-B
Conference
ESC 2024
Type
Peer-reviewed article

7 November 2024 10:55

HELIOS-A: Vutrisiran meets exploratory endpoints

Presented By
Dr Pablo García-Pavía , Hospital Universitario Puerta de Hierro Majadahonda, Spain
Trial
Phase 4, HELIOS-A
Conference
HFA 2022
Type
Peer-reviewed article

28 July 2022 12:16

BCL11A as a novel target in gene therapy for sickle cell disease

Presented By
Dr David Williams, Boston Children’s Hospital, USA
Conference
ASH 2019
Type
Peer-reviewed article

5 March 2020 20:45

New RNAi therapies to reduce triglycerides: 2 studies show favourable results

Presented By
Prof. Christie Ballantyne & Prof. Gerald Watts
Conference
AHA 2019
Type
Peer-reviewed article

26 February 2020 18:06
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