Tag: Enzyme Replacement Therapy

Therapeutic advancement in Pompe disease

Presented By
Prof. Antonio Toscano, University of Messina, Italy
Conference
EAN 2024
Type
News article

25 July 2024 10:52

Sustained benefits of avalglucosidase alfa in late-onset Pompe disease

Presented By
Dr Benedikt Schoser, Ludwig-Maximilians-University of Munich, Germany
Trial
NEO1; NEO-EXT
Conference
EAN 2020
Type
Peer-reviewed article

10 September 2020 14:37
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